September 28, 2025
This short course explores the complexities of evaluating interventions for rare diseases, including limited data, small patient populations, and high costs.
Topics Include:
Key challenges in applying HTA to rare disease contexts
Methodological considerations for limited evidence
Case study example from Europe
Group discussion on current approaches and open issues
Designed for professionals with a basic understanding of HTA who want to strengthen their skills in rare disease evaluation.
LEVEL: Intermediate
TRACK: Health Technology Assessment
This short course is offered in-person at the ISPOR Real-World Evidence Summit 2025 . Separate registration is required. Visit the ISPOR Real-World Evidence Summit 2025 Program page to register and learn more.
FACULTY MEMBERS
Schedule:
LENGTH: 4 Hours | Course runs 1 day
Sunday, 28 September 2025 | Course runs 1 Day
8:00-12:00 Japan Standard Time (JST)
ISPOR short courses are designed to enhance knowledge and techniques in core health economics and outcomes research (HEOR) topics as well as emerging trends in the field. Short courses offer 4 or 8 hours of premium scientific education and an electronic course book. Active attendee participation combined with our expert faculty creates an immersive and impactful learning experience. Short courses are not recorded and are only available during the live course presentation.