PCR198 Psychometric Validation Of The North Star Assessment For Limb-Girdle Type Muscular Dystrophies (NSAD) In Limb-Girdle Muscular Dystrophy Sarcoglycanopathies (LGMD 2C/2D/2E) Using Baseline JOURNEY Data
Abstract
Authors
Intan Purnajo Piper Fromy Linda Lowes Meredith K. James Ivana Filipovic Audhya