EE279 Model-Projected Long-Term Clinical Outcomes of Exagamglogene Autotemcel (exa-cel) Gene-Edited Therapy in Patients with Transfusion-Dependent Beta-Thalassemia in the United Kingdom
Abstract
Authors
C. Udeze S. Jeyakumar H. Fang H. Yang N. Li D. Fattah J. Howard A. Lopez