HTA130 Value Contribution of Olipudase Alfa Therapy for the Treatment of Non-Central Nervous System Manifestations of Acid Sphingomyelinase Deficiency (ASMD) by Multi-Criteria Decision Analysis (MCDA)
Abstract
Authors
MR Abad A González-Meneses E Gras JL Poveda JL Trillo D de Vicente J Villarubia M Baret X Badia