CO20 Predicted Time to Wheelchair and Ventilation Events Comparing Avalglucosidase Alfa (AVA) Versus (vs) Alglucosidase Alfa (ALG) Using a Model of Late-Onset Pompe Disease (LOPD)
Abstract
Authors
M Fournier JJ Caro A Coughlan K Wilson M Roberts AT van der Ploeg ME Kruijshaar KI Berger L Pollissard