PRO12 HOW DOES RISDIPLAM COMPARE IN INFANTILE ONSET SPINAL MUSCOLAR ATROPHY (SMA)? PRELIMINARY INDIRECT TREATMENT COMPARISONS BASED ON FIREFISH PART 1 DATA
Abstract
Authors
M. Daigl A. Kotzeva K. Gorni R. Evans N. Hawkins D.A. Scott A. Mahajan G. Baranello L. Servais