PND9 EVENT-FREE SURVIVAL AND MOTOR MILESTONE ACHIEVEMENT FOLLOWING AVXS-101 AND NUSINERSEN INTERVENTIONS CONTRASTED TO NATURAL HISTORY FOR TYPE I SPINAL MUSCULAR ATROPHY PATIENTS
Abstract
Authors
O. Dabbous D.M. Sproule D.E. Feltner F.G. Ogrinc M. Menier M. Droege B. Maru F. Khan R. Arjunji