PSY18 - RAPID IMPROVEMENTS IN MOTOR FUNCTION IN SPINAL MUSCULAR ATROPHY TYPE 1 FOLLOWING AVXS-101 GENE REPLACEMENT THERAPY
Abstract
Authors
O. Dabbous M. Droege D. Feltner A. Novack M. Menier D. Ryman D.M. Sproule
O. Dabbous M. Droege D. Feltner A. Novack M. Menier D. Ryman D.M. Sproule
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