EE295 Cost-Utility Analysis (CUA) of Sepiapterin for Treatment of Phenylketonuria (PKU)
Abstract
Authors
Rongrong Zhang Anupam Chakrapani Takashi Hamazaki Melissa D. Lah Ania C. Muntau Danielle J. Ruebel Suresh Vijay Roberto T. Zori Francois Feillet Thomas OConnell Jonathan J. Woolley Yixi Teng Marjorie Crowell Ioannis Tomazos