PURPOSE: This workshop will describe recent and novel applications where patients have been engaged to provide qualitative and quantitative data to inform value assessments.

DESCRIPTION: Value assessment is emerging as a key policy lever for pharmaceutical coverage and reimbursement decision-making in the United States. Value frameworks largely rely on traditional value assessment methods such as comparative effectiveness research (CER), literature-based cost-effectiveness analyses (CEAs), and appraisal committees that deliberate the relative value of pharmaceutical interventions. A common critique of these traditional value assessment methods is that they do not represent the full impact of pharmaceutical interventions on patients. Value assessment developers look to health economists for rigorous and appropriate methods to enhance the traditional approaches. However, health economists have not reached a consensus on how to measure and incorporate additional criteria important to patients and broader society into value assessment applications.

This workshop will review recent and novel efforts in patient engagement and the elicitation of patient-centered data to qualitatively and quantitatively inform value assessment. Dr. McQueen will introduce the topic and present recent research from the University of Colorado’s pValue Center on eliciting value criteria from patients with rare diseases. Dr. Oehrlein will provide a background on the National Health Council’s patient engagement experience, including patient group surveys to inform health economic models. Dr. Slejko will present recent research from the University of Maryland’s PAVE Center on disease-agnostic patient-informed value elements among chronic disease patients. Finally, Dr. Whittington will provide an overview of the Institute for Clinical and Economic Review’s growing experience with patient engagement and how patient-centered value criteria may inform health economic models. Each discussant will have 10-15 minutes to address their portion of the workshop. Using ISPOR polling software, audience members will respond to feasibility of approaches presented, along with their own patient engagement experiences for value assessment.