MAIN COMPONENTS OF PUBLIC POLICIES AND FINANCING STRATEGIES ADOPTED BY OECD COUNTRIES TO IMPROVE ACCESS TO DRUGS FOR RARE DISEASES- A SCOPING REVIEW

Author(s)

Quirland-Lazo C1, Paredes Fernandez D1, Lenz Alcayaga R2
1Universidad de Chile, Santiago, Chile, 2Lenz Consultores, Santiago, Chile

BACKGROUND: Since the Orphan Drug Act in United States in 1983, several countries have been implementing courses of action to improve access to Drugs for Rare Diseases (DRD). Despite of the growing body of literature available to describe these efforts, until now, there’s no systematic research in place to characterize and compare the wide range of OECD countrie activities to accomplish their task. OBJECTIVES: Describe the main components of public policies and financing strategies adopted by OECD countries to improve access to DRD. METHODS: We carried out a scoping review through its five first stages. Search strategy considered different sources, as electronic databases (Medline, Embase, Cochrane, CINAHL, LILACS, ECONLIT, Web of Science), key journals (Orphanet Journal of Rare Diseases, and Value in Health), grey literature from different institutions (we consult ISPOR Health Authority by Country inventory to identify their web sites in each OECD countries), and reference lists. The search algorithm was buid using the work of the ISPOR Rare Diseases Groups of Interest on terms and definitions. Categorization and result analysis were performed using the analytical-descriptive method, considering 3 conceptual frameworks: public policy definition (Subirats, 2008), financing function (Kutzin, 2000), and fourth hurdle systems (Hutton, 2006). RESULTS:

Conference/Value in Health Info

2017-05, ISPOR 2017, Boston, MA, USA

Value in Health, Vol. 20, No. 5 (May 2017)

Code

PSY141

Topic

Health Policy & Regulatory, Health Technology Assessment

Topic Subcategory

Approval & Labeling, Decision & Deliberative Processes, Reimbursement & Access Policy

Disease

Rare and Orphan Diseases

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