Meaningful Change Thresholds and Fatigue Severity Points on Patient-Reported Outcomes by the Fatigue Symptoms and Impacts Questionnaire in Patients With Relapsing Multiple Sclerosis

May 1, 2024, 00:00 AM
10.1016/j.jval.2024.02.006
https://www.valueinhealthjournal.com/article/S1098-3015(24)00076-7/fulltext
Section Title : PATIENT-REPORTED OUTCOMES
Section Order : 598
First Page : 598

Objectives

The Fatigue Symptoms and Impacts Questionnaire-Relapsing Multiple Sclerosis (FSIQ-RMS) is a new content-valid, concise, and reliable 20-item patient-reported outcome measure to evaluate the symptoms and impacts of fatigue in patients with relapsing forms of multiple sclerosis. Analyses were performed to derive meaningful change thresholds (MCTs) on patient-reported outcomes as measured by FSIQ-RMS and generate receiver operating characteristic (ROC) curves to determine fatigue severity cut points at baseline and change in severity at post-baseline and supplement the anchor-based MCT results.

Methods

Analyses were based on data from the OPTIMUM trial (NCT02425644). An anchor-based approach using uncollapsed changes on the Patient Global Impression of Severity at week 108 were used to determine the MCT for only the FSIQ-RMS Symptoms domain; distribution-based MCT estimations were conducted using baseline FSIQ-RMS Impacts scores. ROC curves with calculation of area under the curve were used to identify the best cut point.

Results

Based on the evidence provided by the anchor-based analyses using the Patient Global Impression of Severity as an anchor for the FSIQ-RMS Symptoms domain, meaningful score changes for improvement and deterioration were −6.3 and 6.3, respectively. Meaningful score changes for the FSIQ-RMS Physical, Cognitive/Emotional, and Coping Impacts domains using distribution-based methods were 10.8, 8.4, and 9.8, respectively. These results are supported by the ROC analyses.

Conclusions

Thresholds to support interpretation of the FSIQ-RMS, such as MCTs, can be used to determine and categorize patients who have experienced a meaningful change in their MS-related fatigue (eg, responder analyses) in future clinical research studies.

https://www.valueinhealthjournal.com/action/showCitFormats?pii=S1098-3015(24)00076-7&doi=10.1016/j.jval.2024.02.006
HEOR Topics :
  • Clinical Trials
  • Economic Evaluation
  • Musculoskeletal Disorders
  • Patient-Centered Research
  • Patient-reported Outcomes & Quality of Life Outcomes
  • Specific Diseases & Conditions
  • Study Approaches
  • Surveys & Expert Panels
  • Thresholds & Opportunity Cost
Tags :
  • fatigue
  • meaningful change threshold
  • patient-reported outcome
  • relapsing multiple sclerosis
  • symptoms
Regions :
  • Global