May 16-19, 2004, Crystal Gateway Marriott, Arlington, VA

 

PROGRAM: MONDAY, MAY 17TH

8:00AM-8:30AM WELCOME & INTRODUCTION
Mark Sculpher, MSc, PhD, Professor, University of York, Centre for Health Economics, Heslington York

In Memoriam: Bernie O'Brien PhD
Presented by: Michael Drummond PhD, Professor of Economics and Director, Centre for Health Economics, University of York, Heslington, York

PRESIDENTIAL ADDRESS
Sean Sullivan PhD, 2003-2004 ISPOR President & Professor, University of Washington, Seattle, WA, USA

 
8:30AM-9:45AM FIRST PLENARY SESSION

MEDICARE DRUG BENEFIT & COST-EFFECTIVENESS: WHO PLAYS & WHO PAYS

Moderator: Bryan Luce PhD MBA, Chairman of the Board, MEDTAP International, Bethesda, MD, USA

Speakers: Sean Tunis MD, MSc, Chief Medical Officer of CMS & Director, Office of Clinical Standards & Quality, Coverage and Analysis Group, Centers for Medicare and Medicaid Services, Baltimore, MD, USA; Jean Slutsky PA, MSPH, Acting Director, Center for Outcomes and Evidence, Agency for Healthcare Research and Quality (AHRQ), Rockville, MD, USA

This plenary session will address US legislation concerning Medicare Drug Benefit Plan and the use of cost-effectiveness and outcomes research information in drug selection decisions. The role of the Agency for Health Care Research and Quality and the National Institutes of Health, as well as the Food and Drug Administration in providing and regulating this information will be discussed.

 

9:45AM-10:15AM EXHIBITS & CONTRIBUTED POSTER PRESENTATIONS VIEWING – SESSION I
 
10:15AM-11:15AM CONTRIBUTED PODIUM PRESENTATIONS – SESSION I
  Pharmacoeconomics/health economic, quality-of-life, and outcomes research study results for the following diseases will be presented:
 
Cardiovascular Disease 

CV1
HEALTH PREFERENCES AFTER CABG OR PCI FOLLOWING AN ACUTE MYOCARDIAL INFARCTION

Radeva J, Reed S, Weinfurt K, Anstrom K, Velazquez E, Schulman K
Duke Clinical Research Institute, Durham, NC, USA
 

CV2
CARDIOVASCULAR RISK OF SELECTIVE CYCLOOXYGENASE-2 INHIBITORS COMPARED TO OTHER NONSTEROIDAL ANTI-INFLAMMATORY AGENTS: AN OBSERVATIONAL STUDY OF A MEDICAID POPULATION
Shaya FT, Blume SW, Blanchette CM, Mullins CD, Weir MR
University of Maryland, Baltimore, MD, USA
 

CV3
THE USE OF A PROBABILISTIC DECISION MODEL TO ASSESS THE COST-EFFECTIVENESS OF DRUG-ELUTING STENTS IN ALTERNATIVE PATIENT SUB-GROUPS
Sculpher M, Hawkins NS1
1University of York, York, United Kingdom

CV4
LOWER CARDIOVASCULAR RISK ASSOCIATED WITH PIOGLITAZONE MONOTHERAPY COMPARED TO INSULIN MONOTHERAPY: A RETROSPECTIVE PROPENSITY SCORE MATCHED COHORT STUDY
Iyer S1, Xu Y1, Rosenson R2, Rajagopalan R1
1Takeda Pharmaceuticals North America Inc, Lincolnshire, IL, USA; 2Northwestern University, Feinberg School of Medicine, Chicago, IL, USA

Cancer 

CN1
THE STATE OF THE SCIENCE OF HRQOL ASSESSMENT IN CANCER: FINDINGS FROM THE CANCER OUTCOMES MEASUREMENT WORKING GROUP
Lipscomb J1, Gotay C2, Snyder C1
1National Cancer Institute, Bethesda, MD, USA; 2Cancer Research Center of Hawaii, Honolulu, HI, USA
 

CN2
COST-EFFECTIVENESS OF DIAGNOSTIC, STAGING, AND TREATMENT OPTIONS FOR MELANOMA
Chavez YE1, Lee WC2, Botteman MF3, Pashos CL4
1Abt Associates, Inc, Bethesda, MD, USA; 2Abt Associates Inc. - HERQuLES, Bethesda, MD, USA; 3Abt Associates Inc. - HERQuLES, Cambridge, MA, USA; 4Abt Associates Inc, Cambridge, MA, USA
 

CN3
COST-EFFECTIVENESS OF ANASTROZOLE VS TAMOXIFEN AS ADJUVANT THERAPY IN POSTMENOPAUSAL WOMEN WITH EARLY BREAST CANCER (EBC): A UK NATIONAL HEALTH SERVICE (NHS) PERSPECTIVE
Benedict Á1, Mansel on behalf of the ATAC Trialists' Group R2
1MEDTAP International Inc, London, United Kingdom; 2University of Wales College of Medicine, Cardiff, United Kingdom
 

CN4
COST-EFFECTIVENESS (CE) ANALYSIS OF INTERFERON-ALPHA IN HIGH-RISK MELANOMA PATIENTS
Ding M1, Xing Y2, Shih T2, Cox D1, Cantor S2, Cormier J2
1Rice University, Houston, TX, USA; 2The University of Texas M.D. Anderson Cancer Center, Houston, TX, USA

Respiratory Disorders and Infections 

RI1
THE EFFECT OF PRESCRIPTION DRUG COVERAGE ON THE COST OF CARE FOR MEDICARE BENEFICIARIES WITH ASTHMA
Atherly A, Williams S, Redd S
Centers for Disease Control, Atlanta, GA, USA
 

RI2
THE EXCESS COST OF CHRONIC OBSTRUCTIVE PULMONARY DISEASE FROM A MANAGED-CARE PERSPECTIVE
Boulanger L1, Marton JP2, Friedman M1, Dixon D1, Menzin J1
1Boston Health Economics, Inc, Waltham, MA, USA; 2Pfizer US Outcomes Research Group, New York, NY, USA
 

RI3
COST-EFFECTIVENESS OF INFLUENZA VACCINE IN 6-24 MONTH OLD CHILDREN
Woolcott JC1, Marra F1, Brunham RC2
1BC Centre for Disease Control, Vancouver, BC, Canada; 2University of British Columbia Centre for Disease Control, Vancouver, BC, Canada
 

RI4
AN ECONOMIC ANALYSIS OF RAPID TESTS AND ANTIVIRAL TREATMENTS FOR INFLUENZA IN CHILDREN
Prosser LA1, Uyeki TM2, Bridges CB2, Rego VH1, Meltzer M2, Schwartz B2, Thompson WW2, Fukuda K2, Lieu TA1
1Harvard Medical School and Harvard Pilgrim Health Care, Boston, MA, USA; 2CDC, Atlanta, GA, USA

Arthritis

AR1
ASSESSING THE COST-EFFECTIVENESS OF COX-2 SPECIFIC INHIBITORS FOR ARTHRITIS IN THE VETERANS HEALTH ADMINISTRATION
Schaefer M1, DeLattre M1, Gao X2, Stephens J2, Botteman M2, Morreale A1
1VA San Diego Health care System, San Diego, CA, USA; 2Abt Associates Clinical Trials, Bethesda, MD, USA

AR2
A COST-EFFECTIVENESS ANALYSIS OF BIOLOGICAL TREATMENTS FOR RHEUMATOID ARTHRITIS
Chiou CF1, Wanke L2, Yu E2, Ofman J2
1Zynx Health, A Cerner Company, Beverly Hills, CA, USA; 2Amgen, Inc, Thousand Oaks, CA, USA
 

AR3
REVALIDATION OF THE ORIGINAL CEDARS-SINAI RHEUMATOID ARTHRITIS HEALTH-RELATED QUALITY OF LIFE (CSHQ-RA) INSTRUMENT
Chiou CF1, Sherbourne C2, Cornelio IL3, Lubeck D3, Paulus H4, Dylan M1, Weisman M5
1Zynx Health, A Cerner Company, Beverly Hills, CA, USA; 2RAND Corporation, Santa Monica, CA, USA; 3Amgen, Inc, Thousand Oaks, CA, USA; 4UCLA, Los Angeles, CA, USA; 5Cedars-Sinai Health System, Los Angeles, CA, USA

AR4
THE DEVELOPMENT OF PROPENSITY SCORES FROM ADMINISTRATIVE DATABASES FOR THE ANALYSIS OF THE EFFECTIVENESS OF AN OSTEOARTHRITIS ACADEMIC DETAILING SERVICE ON PRESCRIBING BEHAVIOUR
Graham SD, Hartzema AG
University of Florida, Gainesville, FL, USA

11:15AM-11:30AM BREAK
11:30AM-12:30PM ISSUES PANELS – SESSION I
  EFFECT OF SECTION 1013 "RESEARCH ON OUTCOMES OF HEALTH CARE ITEMS AND SERVICES" OF THE US MEDICARE MODERNIZATION ACT ON OUTCOMES RESEARCH

MODERATOR: Jean Paul Gagnon PhD, Director Public Policy, Aventis Pharmaceuticals Inc., Bridgewater, NJ, USA
PANELISTS: Jean R. Slutsky, PA, MSPH, Acting Director, Center for Outcomes and Evidence, Agency for Healthcare Research and Quality (AHRQ), Rockville, MD, USA, Kathleen Lohr PhD, Co-Director, RTI-UNC Evidence-based Practice Center, Research Triangle Park, NC, USA; John Santa MD, Former Administrator, Office of Oregon Health Policy and Research, Portland, OR, USA

STRATIFIED COST-EFFECTIVENESS ANALYSIS: THE RISKS AND REWARD OF LOOKING AT SUB-GROUPS

MODERATOR: Henry Glick PhD, Health Economist, University of Pennsylvania, Division of Internal Medicine, Philadelphia, PA, USA

PANELISTS:
Jeffrey Hoch PhD, Assistant Professor, University of Western Ontario, Department of Epidemiology and Biostatistics, London, ON, Canada; Andrew Willan PhD, Professor, Department of Public Health Sciences, University of Toronto, Toronto, ON, Canada; Joseph Heyse PhD, Executive Director, Merck Research Laboratories, Biostatistics and Research Data Systems, West Point, PA, USA; John Cook PhD, Health Economics, Merck Research Laboratories, Blue Bell, PA, USA

RISK SHARING DEALS IN THE REAL WORLD: CAN WE AFFORD THEM AND DO THEY WORK?

MODERATOR: Charles Petrie PhD, Sr. Director/Team Leader, Outcomes Research Group, Pfizer Inc, Groton, CT, USA;


PANELISTS: Adrian Towse MA, Director, Office of Health Economics, London, UK;
Maureen Mangotich MD, MPH, Medical Director, State Initiatives, Pfizer Health Solutions, Santa Monica, CA


COST ATTRIBUTION IN ECONOMIC EVALUATION: WHAT IS SIGNAL AND WHAT IS NOISE?

MODERATORS: Teresa Kauf PhD,
Research Assistant Professor, Center for Clinical and Genetic Economics, Duke Clinical Research Institute, Durham, NC, USA

PANELISTS: Gerry Oster PhD, Vice President, PAI, Brookline, MA, USA; Daniel Polsky PhD, Research Associate Professor, General Internal Medicine, University of Pennsylvania, Philadelphia, PA, USA


INDUSTRY AND REGULATORY PERSPECTIVES ON TRANSLATING PATIENT REPORTED OUTCOME MEASURES

MODERATOR: Joyce Cramer BS, Yale University, New Haven, CT, USA
PANELISTS: Laurie Burke RPh, Director, Study Endpoints and Label Division, U.S. Food and Drug Administration, Rockville, MD, USA; Richard J. Willke PhD, Senior Director/Group Leader, Worldwide Outcomes Research, Pfizer Inc., Peapack, NJ, USA; Diane Wild MSc, Director, Oxford Outcomes, Cassington, Oxford, UK
 

12:30AM-2:00PM LUNCH, EXHIBITS & GRAND OPENING OFCONTRIBUTED POSTER PRESENTATIONS VIEWING – SESSION I
2:00PM-3:00PM CONTRIBUTED WORKSHOPS – SESSION I

Clinical study methodology issues including pharmacoepidemiology

W1: PATIENT REPORTED OUTCOME AND RESOURCE USE DATA IN CLINICAL TRIALS: GOING BEYOND TREATMENT GROUP COMPARISONS

Compliance issues

W2: PATIENT COMPLIANCE AND PERSISTENCE WITH PRESCRIBED MEDICATION: MEASUREMENT AND HEALTH ECONOMIC IMPACT

Cost study methodology issues

W3: USE AND INTEGRATION OF FREELY AVAILABLE U.S. PUBLIC USE FILES TO ANSWER PHARMACOECONOMIC QUESTIONS: DECIPHERING THE ALPHABET SOUP

Formulary development research issues

W4: MANAGED CARE DATA: TOOLS AND METRICS FOR FORMULARY DEVELOPMENT

Healthcare policy development issues using outcomes research

W5: SYSTEMATIC REVIEWS OF COST-EFFECTIVENESS ANALYSES USING ELECTRONIC AND WEB-BASED REGISTRIES

Preference-based studies methodology issues including utility studies

W6: ADVANCES IN MAPPING HEALTH-RELATED QUALITY OF LIFE: AN EQ-5D INDEX BASED ON SF-36 DATA

Quality of life study methodology issues including patient reported outcomes

W7: APPLYING ITEM RESPONSE THEORY MODELING FOR IMPROVING HEALTH OUTCOMES MEASUREMENT

Risk assessment/risk management issues

W8: THERAPEUTIC EXPANSION OF THE CLASSICAL Q-TWIST APPROACH
 

3:00PM-3:15PM BREAK
3:15PM-4:15PM CONTRIBUTED WORKSHOPS – SESSION II
  Clinical study methodology issues including pharmacoepidemiology

W9: JOURNEY TOWARDS A TRUE EFFECT IN COHORT STUDIES: OBSTACLES, STATISTICAL TOOLS, AND “DIFFERENCE IN DIFFERENCE” ESTIMATES

Compliance issues

W10: METHODS IN COMPLIANCE EVALUATION: DETERMINING AND ANALYZING APPROPRIATE MEASURES

Cost study methodology issues

W11: AT THE FRONTIER: MAXIMZING THE VALUE OF CLAIMS DATA

Formulary development research issues

W12: THE FORMULARY DECISION PROCESS: WHAT KIND OF INFORMATION IS TRULY HELPFUL?

Healthcare policy development issues using outcomes research

W13: THE USE OF DISCRETE EVENT SIMULATION TO ASSESS THE VALUE OF HEALTH CARE INTERVENTIONS

Preference-based studies methodology issues including utility studies

W14: INCORPORATING PREFERENCES INTO OUTCOME MEASURES FOR THE VALUATION OF GENETIC BASED SERVICES

Quality of life study methodology issues including patient reported outcomes

W15: SELECTING OUTCOME MEASURES FOR INTERVENTION STUDIES: MAXIMIZING USE OF WEB-BASED RESOURCES

Risk assessment/risk management issues

W16: CAPTURING THE VALUE OF PHARMACEUTICALS: THE ROLE OF OUTCOMES RESEARCH IN PRICING DECISIONS
 

4:15PM-4:30PM BREAK
4:30PM-5:30PM ISPOR FORUMS
  • Student Forum
• Compliance Special Interest Group Forum

 

 

Quality of Life Special Interest Group Forum

4:30PM-4:35PM

Emerging Issues in PRO Research: This session will examine major applied research issues that are important for the development and use QoL and patient reported outcome (PRO) measures. The discussion will identify other areas that might also be added to a PRO/QoL research agenda and begin a dialog concerning ISPOR’s role in furthering advances in applied PRO research.

Moderator: Pennifer Erickson PhD, Co-founder, O.L.G.A., State College, PA, USA
 
4:35PM -4:50PM Instrument Development and Validation: How Much is Enough?

Speaker: Margaret Rothman PhD, Executive Director, HE&P, PGSM, Johnson & Johnson Pharmaceutical Services, LLC, Raritan, NJ, USA
 

4:50PM -5:05PM

 
The MCID and PRO Research: Should We Draw a Line in the Sand?

Speaker: Nancy Kline Leidy PhD, President and CEO, MEDTAP International, Bethesda, MD, USA
 

5:05PM -5:15PM

 
Discussion of Current Research Issues: What’s Hot? What’s Not?
Speaker: Pennifer Erickson PhD, Co-founder, O.L.G.A., State College, PA, USA
 
5:15PM -5:30PM Discussion
 
5:30PM-6:30PM

ISPOR Medication Compliance SIG Open Meeting

ISPOR Clinical Practice SIG Open Meeting

ISPOR Annual Business Meeting
6:00PM-8:00PMM EXHIBITORS’ OPEN HOUSE RECEPTION & CONTRIBUTED POSTER PRESENTATION – SESSION I
   

9th Annual International Meeting Main Page

 

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